Quince Overview - Learn about the company’s pioneering Autologous Intracellular
Drug Encapsulation (AIDE) technology designed to chronically deliver corticosteroids without toxicity and the potential to transform treatment paradigms across multiple rare disease indications where corticosteroids are the standard of care.
Technology Deep Dive - A look at the company’s proprietary eDSP System, which is a unique drug/device combination that uses an automated process designed to encapsulate dexamethasone sodium phosphate (eDSP) into a patient’s own red blood cells to allow for the chronic, monthly administration of corticosteroids without toxicity.
Lead Indication: Ataxia-Telangiectasia (A-T) - Insights into this devastating pediatric rare disease, encouraging prior ATTeST study results, and the company’s fully enrolled pivotal Phase 3 NEAT clinical trial with topline results expected in the first quarter of 2026.
Mechanism of Action - Learn about multiple synergistic mechanisms of action that support eDSP’s efficacy and disease modifying activity while mitigating corticosteroid toxicity, and how transcriptomic profiling reveals novel insights and potential biomarkers in A-T.
Regulatory Overview - Discussion of the company’s Special Protocol Assessment (SPA) agreement in place with the U.S. Food and Drug Administration (FDA), orphan drug and Fast Track designations for the treatment of A-T, and the anticipated regulatory approval pathway for eDSP, assuming positive NEAT study results.
Commercial Development - Insights into the company’s attractive commercial opportunity and launch preparedness planning for eDSP, including details of its recently announced strategic relationship with Option Care Health.
Driving Value Creation - A look at the company’s strong competitive positioning, significant opportunity to quickly expand its development pipeline into additional high-value, rare disease indications like Duchenne muscular dystrophy, and its existing cash runway which provides funding through topline results and into the second quarter of 2026.
Q&A Session - Delve into the details during a Q&A session with Quince's leadership team following the conclusion of formal presentations.
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Dirk Thye, M.D., has served as Quince Therapeutics’ CEO and Board Member since May 2022 and as Chief Medical Officer since December 2023, bringing nearly 25 years of biotechnology experience across drug discovery, R&D, and executive leadership. He has led FDA approval for multiple drug programs across therapeutic areas such as infectious diseases, oncology, CRISPR, and metabolic diseases. MORE BIO INFO
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Charles Ryan has served as Quince Therapeutics’ President since September 2023, overseeing corporate legal activities, intellectual property, international integration of operations, and business functions, including the planned acquisition of EryDel SpA. MORE BIO INFO
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Brendan Hannah has served as Quince’s Chief Operating Officer since October 2023, its Chief Business Officer since May 2022, and is currently the company’s Principal Financial Officer. To this role, he brings 15 years of corporate development, operational, finance, and company formation experience. MORE BIO INFO
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Giovanni Mambrini has served as Quince's Chief Technology Officer since October 2023, bringing more than 25 years of medical device technology experience with cross-functional expertise in bringing complex programs to market, including experience securing Conformite Europeene (CE) mark and FDA regulatory approval for several innovative device products. MORE BIO INFO
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Pamela Williamson has served as Quince's Head of Regulatory Affairs since July 2023, bringing more than 30 years of global leadership experience, inclusing a strong track record in the successful development and registration of products to treat patients with serious and life-threatening rare diseases. MORE BIO INFO
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Caralee Schaefer, Ph.D., has served as Quince’ Vice President, Nonclinical Development since August 2024. To this role, as a translational research scientist, she brings more than 25 years of nonclinical development experience, with a particular focus on inflammation, autoimmunity, fibrosis, and rare disease research. MORE BIO INFO
Quince Therapeutics is a late-stage biotechnology company dedicated to unlocking the power of a patient’s own biology for the treatment of rare diseases.
Our Phase 3 lead asset, eDSP, is the first product in development that leverages our proprietary Autologous Intracellular Drug Encapsulation, or AIDE, technology platform, which is a novel drug/device combination that uses an automated process designed to encapsulate a drug into the patient’s own red blood cells. eDSP is composed of dexamethasone sodium phosphate (DSP) encapsulated in autologous red blood cells targeted to treat a rare pediatric neurodegenerative disease called Ataxia-Telangiectasia, or A-T. DSP is a corticosteroid well-described for its anti-inflammatory properties, but is coupled with serious adverse effects, including potential long-term adverse effects due to adrenal suppression. eDSP is designed to maintain the efficacy of corticosteroids while mitigating toxicity associated with conventional corticosteroid treatment.
In July 2025, Quince completed enrollment of our pivotal Phase 3 NEAT clinical trial, which is an international, multi-center, randomized, double-blind, placebo-controlled clinical trial evaluating the neurological effects of eDSP in patients with A-T. We expect to report topline results in the first quarter of 2026.
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